In vivo lentiviral vector gene therapy to cure hereditary tyrosinemia type 1 and prevent development of precancerous and cancerous lesions
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Analysis of LV biodistribution by real-time quantitative PCR (RT-qPCR).
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Lentiviral vectors for inducible, transactivator-free advanced therapy medicinal products: Application to CAR-T cells: Molecular Therapy - Nucleic Acids
Self-organized and directed branching results in optimal coverage in developing dermal lymphatic networks
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